All journal news
PRiORiTy Usability Study
Published: 29/01/2025
Lessons Learnt and Share Learnings at the EFGCP Annual Paediatric Conferences
Published: 13/01/2025
A matrix tool to foster patient engagement in children, adolescents and young adults: report from a multistakeholder workshop
Published: 12/12/2024
Better Medicines for Children: Lessons Learnt and Share Learnings at the EFGCP Annual Paediatric Conferences
Published: 14/11/2024
Using facial reaction analysis and machine learning to objectively assess palatability of medicines in children
Published: 09/10/2024
Feasibility of an App-Assisted and Home-Based Video Version of the Timed up and Go Test for Patients with Parkinson’s Disease: vTUG
Published: 03/10/2024
Video-based assessments of activities of daily living: generating real-world evidence in pediatric rare diseases
Published: 10/06/2024
The Digital 1-Minute Walk Test: A New Patient-centered Cardiorespiratory Endpoint
Published: 05/04/2024
Recommendations to address respondent burden associated with PROs
Published: 01/03/2024
A patient-centred and multi-stakeholder co-designed observational prospective study protocol: Example of the adolescent experience of treatment for X-linked hypophosphataemia (XLH)
Published: 22/01/2024
Development and usability testing of an ePRO solution for patients with inflammatory diseases in an ATMP basket trial
Published: 11/10/2023
A pilot study of a digital 1-Minute Walk Test as a novel decentralised endpoint in pulmonary hypertension research
Published: 30/09/2023
SARAhome video assessment deployed in pan-European ataxia observational study
Published: 22/08/2023
Accelerometer-derived sleep measures in idiopathic dystonia
Published: 15/08/2023
A global neuronopathic Gaucher disease registry (GaRDIAN): a patient-led initiative
Published: 28/07/2023